|Study marks the emergence of disease-modifying treatments for autism spectrum disorders|
|December 16, 2010|
|Boston, Mass. -- Researchers at Children's Hospital Boston have begun a randomized, placebo-controlled trial to test a potential drug treatment for Rett syndrome, the leading known genetic cause of autism in girls. The drug, mecasermin, a synthetic form of insulin-like growth factor-1 (IGF-1), is already FDA-approved for children with short stature due to IGF-1 deficiency.|
Spotlight Series: Rett Boys! - We are so excited to continue to highlight an extremely important group of people in our Rett family, our Rett BOYS! Read on to hear Maja and her son Tobi...
2 weeks ago