|Study marks the emergence of disease-modifying treatments for autism spectrum disorders|
|December 16, 2010|
|Boston, Mass. -- Researchers at Children's Hospital Boston have begun a randomized, placebo-controlled trial to test a potential drug treatment for Rett syndrome, the leading known genetic cause of autism in girls. The drug, mecasermin, a synthetic form of insulin-like growth factor-1 (IGF-1), is already FDA-approved for children with short stature due to IGF-1 deficiency.|
Understanding Breathing problems in Rett Syndrome - Breathing problems are a major challenge in patients with Rett syndrome (RS) and they are more apparent in day-time but irregular breathing issues can be ...
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