|Study marks the emergence of disease-modifying treatments for autism spectrum disorders|
|December 16, 2010|
|Boston, Mass. -- Researchers at Children's Hospital Boston have begun a randomized, placebo-controlled trial to test a potential drug treatment for Rett syndrome, the leading known genetic cause of autism in girls. The drug, mecasermin, a synthetic form of insulin-like growth factor-1 (IGF-1), is already FDA-approved for children with short stature due to IGF-1 deficiency.|
Spotlight Series: Renee - Meet Renee who is 36 and her mom Rose. They have been on this Rett Syndrome journey for quite some time and have some great advice to share with all of us....
1 week ago